Cocktail number AO-one AO-two
1 1. Hi47A(-05+20) 2. Hi47A(+22+46)
2 1. Hi47A(-05+20) 10. Hi47A(+47+72)
3 2. Hi47A(+22+46) 6. Hi47A(-10+15)
4 2. Hi47A(+22+46) 8. Hi47A(-20+5)
5 2. Hi47A(+22+46) 9. Hi47A(-25-01)
6 3. Hi47D(+11-14) 4. Hi47A(+05+29)
7 3. Hi47D(+11-14) 6. Hi47A(-10+15)
8 3. Hi47D(+11-14) 8. Hi47A(-20+5)
Table 2: AO cocktails targeting DMD pseudo-exon in intron 47.