Disease Condition Therapeutic outcome achieved
Sickle cell disease Improvement of hematopoiesis at functional and physiological levels
Hemophilia A - Survival benefit obtained
- Decreased clotting time achieved
Parkinson's disease Dopamine production enhanced, leading to symptomatic improvement
Ischemic heart disease In situ tissue repair leading to improved cardiac performance
Table 8: Models of diseases treated with iPSC-based interventions.