Disease Condition |
Therapeutic outcome achieved |
Sickle cell disease |
Improvement of hematopoiesis at functional and physiological levels |
Hemophilia A |
- Survival benefit obtained
- Decreased clotting time achieved |
Parkinson's disease |
Dopamine production enhanced, leading to symptomatic improvement |
Ischemic heart disease |
In situ tissue repair leading to improved cardiac performance |