Challenges in Rare Diseases Treatment

There are around 7,000 rare diseases, which from a regulatory outlook are defined as those diseases where there are less than 200,000 patients in the US or that affect no more than five in 10,000 of the general population in the EU. Orphan drugs are medicinal products envisioned for diagnosis, prevention and treatment of life-threatening rare diseases. They are "orphans" because the pharmaceutical industry has little interest under normal market conditions in developing and marketing drugs intended for only a small number of patients suffering from very rare conditions.

  • Different types of rare diseases
  • Misperceptions about rare diseases
  • Role of Patient Registries
  • Regulatory Approaches and Alternative Methodologies
  • Rising Patient Costs
  • Reimbursement Strategies

Related Conference of Challenges in Rare Diseases Treatment

August 20-21, 2018

Annual Meeting on Infectious Diseases

Prague, Czech Republic
August 20-21, 2018

Global HIV/AIDS Congress

Prague, Czech Republic
August 27-28, 2018

6th World Congress on Control and Prevention of HIV/AIDS, STDs & STIs

Hilton Zurich Airport, Zurich, Switzerland
August 27-28, 2018

9th International Conference on Emerging Infectious Diseases

Hilton Zurich Airport, Zurich, Switzerland
August 29-30, 2018

5th Annual Congress on Rare Diseases and Orphan Drugs

Boston, Massachusetts, USA
August 29-30, 2018

4th Annual Congress on Infectious Diseases

Boston, Massachusetts, USA
September 03-04, 2018

Global Experts Meeting on Infectious Diseases

Tokyo,Japan
September 27-29, 2018

10th Euro-Global Conference on Infectious Diseases

Rome, Italy
(Holiday Inn Rome Eur Parco dei Medici)
November 6-7, 2018

Global Experts Meet on STD-AIDS and Infectious Diseases

Auckland, New Zealand
November 12-13, 2018

11th Global Infections Conference

Melbourne, Australia
November 15-16, 2018

6th Annual Conference on Parasitology & Infectious Diseases

Istanbul, Turkey
November 22-23, 2018

8th International Conference on Bacteriology and Infectious Diseases

Cape Town, South Africa
Dec 05-06, 2018

6th International Conference On Infectious Diseases

Lisbon, Portugal
December 05-07, 2018

World Congress on Rare Diseases

Dubai, UAE
December 6-7, 2018

14th World Congress on Infection Prevention and Control

Valencia, Spain
Feb 25-26, 2019

6th International Congress on Infectious Diseases

London, United Kingdom

Challenges in Rare Diseases Treatment Conference Speakers

Recommended Sessions

Related Journals

Are you interested in